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Annapoorna Kannan, Kanchan Bhatia, Xiaoting Jiang +7 more · 2026 · Brain communications · Oxford University Press · added 2026-04-24
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder caused by mutation of the
no PDF DOI: 10.1093/braincomms/fcag111
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