👤 M Teresa Magone
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Prospective pilot safety, feasibility study of an optic-to-audio device for children with CLN3 disease.
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Thuy Tien Nguyen
,
Andrea Munoz
,
Kisha Jenkins
+11 more
· 2026 · Orphanet journal of rare diseases · BioMed Central
· added 2026-04-24
Thuy Tien Nguyen
,
Andrea Munoz
,
Kisha Jenkins
,
Ibukun Agbede
,
Wadih M Zein
,
Laryssa A Huryn
,
Brian P Brooks
,
Jennifer Chisholm
,
Julie Christensen
,
Christopher Zalewski
,
M Teresa Magone
,
Colby Chlebowski
,
Audrey Thurm
,
An N Dang Do
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DOI:
10.1186/s13023-026-04319-0
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CLN3
1