👤 Cassandra Dennys-Rivers
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Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease.
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Tyler B Johnson
,
Jon J Brudvig
,
Shibi Likhite
+12 more
· 2023 · Frontiers in genetics · Frontiers
· added 2026-04-24
Tyler B Johnson
,
Jon J Brudvig
,
Shibi Likhite
,
Melissa A Pratt
,
Katherine A White
,
Jacob T Cain
,
Clarissa D Booth
,
Derek J Timm
,
Samantha S Davis
,
Brandon Meyerink
,
Ricardo Pineda
,
Cassandra Dennys-Rivers
,
Brian K Kaspar
,
Kathrin Meyer
,
Jill M Weimer
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CLN3 disease, caused by biallelic mutations in the
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DOI:
10.3389/fgene.2023.1118649
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CLN3
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