👤 Brian K Kaspar

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Articles

articles

Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease.

Tyler B Johnson, Jon J Brudvig, Shibi Likhite +12 more · 2023 · Frontiers in genetics · Frontiers · added 2026-04-24

Tyler B Johnson, Jon J Brudvig, Shibi Likhite, Melissa A Pratt, Katherine A White, Jacob T Cain, Clarissa D Booth, Derek J Timm, Samantha S Davis, Brandon Meyerink, Ricardo Pineda, Cassandra Dennys-Rivers, Brian K Kaspar, Kathrin Meyer, Jill M Weimer Show less

CLN3 disease, caused by biallelic mutations in the

📄 PDF DOI: 10.3389/fgene.2023.1118649

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